NCT04988867API RE2T
An Open-Label Study of Trofinetide for Girls Two to Five Years of Age With Rett Syndrome
This study investigates the safety and tolerability of long-term oral trofinetide treatment in girls with Rett syndrome.
Study ended earlyINTERVENTIONAL
Record summary
This study investigates the safety and tolerability of long-term oral trofinetide treatment in girls with Rett syndrome.
What this record cannot establish
Registry data requiring human review; it cannot determine eligibility or individual benefit.
Study level
Documented countryUS
Centre level7 Sites named in the sources
Original sourceClinicalTrials.gov
Human reviewHuman-reviewed
Centre level
Centre level · 7 Sites named in the sources · US
University of Alabama at Birmingham · Birmingham · USSite opening to confirm
Children's Hospital Colorado · Aurora · USSite opening to confirm
Rush University Medical Center · Chicago · USSite opening to confirm
Boston Children's Hospital/Harvard Medical School · Boston · USSite opening to confirm
Gillette Children's Hospital · Saint Paul · USSite opening to confirm
Washington University · St Louis · USSite opening to confirm
Vanderbilt University Medical Center · Nashville · USSite opening to confirm
Source and review
Résumé ou traduction assisté par IA : peut contenir des erreurs et ne remplace ni une relecture humaine ni un avis médical.
Source updated · Sep 24, 2024
Source updated · Sep 23, 2024
Synced · Sep 19, 2026
Published · Sep 19, 2026
Human review · Sep 19, 2026