Gene therapy: why control the amount of MECP2?
Understanding a preclinical paper on NGN‑401.
Science Translational Medicine · PMID 40173263
Reading room
Understand more, one article at a time.
A selection of real publications, not a complete latest-news feed. The year and study type remain visible.
Trofinetide in young girls: what does DAFFODIL show?
An open-label study in 15 girls aged 2–4.
Med · PMID 40043705
LAVENDER: reading results alongside tolerability.
A 12-week comparative trial, published in 2023.
Nature Medicine · PMID 37291210
Sources and approach
Each record links to its references. The public catalogue is synchronized from ClinicalTrials.gov and shows the source date, its limits and the review status.